Advice

following an abbreviated submission:

vanzacaftor/tezacaftor/deutivacaftor (Alyftrek®) is accepted for restricted use within NHSScotland.

Indication under review: for the treatment of cystic fibrosis (CF) in people aged 6 years and older who have at least one F508del mutation or another responsive mutation in the cystic fibrosis transmembrane conductance regulator (CFTR) gene.

SMC restriction: patients aged 6 years and older who have at least one F508del mutation in the CFTR gene.

Vanzacaftor/tezacaftor/deutivacaftor (Alyftrek®) offers an additional treatment choice in the therapeutic class of CFTR modulators.

This advice applies only in the context of an approved NHSScotland Patient Access Scheme (PAS) arrangement delivering the cost-effectiveness results upon which the decision was based, or a PAS/ list price that is equivalent or lower.

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Medicine details

Medicine name:
vanzacaftor / tezacaftor / deutivacaftor (Alyftrek)
SMC ID:
SMC2800
Indication:

For the treatment of cystic fibrosis (CF) in people aged 6 years and older who have at least one F508del mutation or another responsive mutation in the cystic fibrosis transmembrane conductance regulator (CFTR) gene.

Pharmaceutical company
Vertex Pharmaceuticals Ltd
BNF chapter
Respiratory system
Submission type
Abbreviated
Status
Restricted
Date advice published
09 March 2026